Baby KJ's doctors plan to ask the FDA to approve a clinical trial for a pioneering gene editing approach this winter.
The trial would be open to patients with seven different urea cycle disorders, offering new hope for those affected.
"This is what we thought we would never get,"
Kyle Muldoon, Baby KJ's father, expressed his emotions as he watched a football game with his son, cherishing the ordinary moments they share.
A clinical trial for a new gene editing approach may bring new possibilities for Baby KJ and others with rare diseases.
Author's summary: Baby KJ's doctors to request FDA approval for gene editing trial.